SpliceBio is tackling one of gene therapy’s biggest bottlenecks—the AAV size limit—using a clever protein splicing trick. If it works, this could unlock gene therapies for longer payload, like CFTR.
What I Read This Week: SpliceBio and the…
SpliceBio is tackling one of gene therapy’s biggest bottlenecks—the AAV size limit—using a clever protein splicing trick. If it works, this could unlock gene therapies for longer payload, like CFTR.